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BRIEF-Intellia And Regeneron Announce Clinical Data For NTLA-2001

Reuters2021-06-26

June 26 (Reuters) - Regeneron Pharmaceuticals Inc :

* INTELLIA AND REGENERON ANNOUNCE LANDMARK CLINICAL DATA SHOWING DEEP REDUCTION IN DISEASE-CAUSING PROTEIN AFTER SINGLE INFUSION OF NTLA-2001, AN INVESTIGATIONAL CRISPR THERAPY FOR TRANSTHYRETIN (ATTR) AMYLOIDOSIS

* REGENERON PHARMACEUTICALS - INTERIM READOUT IN ONGOING PHASE 1 TRIAL FINDS SINGLE 0.3 MG/KG DOSE OF NTLA-2001 LED TO 87% MEAN REDUCTION IN SERUM TTR

* NO SERIOUS ADVERSE EVENTS OBSERVED IN FIRST SIX PATIENTS BY DAY 28

Source text for Eikon: Further company coverage:

((Reuters.Briefs@thomsonreuters.com;))

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  • SKYK
    ·2021-06-27
    Intla!
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