辉瑞遗传性凝血障碍基因疗法后期试验成功

华尔街见闻07-25 03:05

美东时间7月25日周三，美国制药巨头辉瑞公司宣布，其针对罕见遗传性凝血障碍——血友病A的实验性基因疗法，在一项大型的后期临床试验中取得了成功。这一成果为该疗法的潜在获批铺平了道路。这种针对A型血友病的疗法，可能成为辉瑞继4月获批用于B型血友病的“Beqvez”之后，该公司进入美国市场的第二种基因疗法。该疗法由辉瑞与Sangamo Therapeutics联合开发。消息发布后，Sangamo ...

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href=https://wallstreetcn.com/articles/3720987><strong>华尔街见闻</strong></a>\n\n\n</h4>\n\n</header>\n<article>\n<div>\n<p>美东时间7月25日周三，美国制药巨头辉瑞公司宣布，其针对罕见遗传性凝血障碍——血友病A的实验性基因疗法，在一项大型的后期临床试验中取得了成功。这一成果为该疗法的潜在获批铺平了道路。\n这种针对A型血友病的疗法，可能成为辉瑞继4月获批用于B型血友病的“Beqvez”之后，该公司进入美国市场的第二种基因疗法。\n该疗法由辉瑞与Sangamo Therapeutics联合开发。消息发布后，Sangamo ...</p>\n\n<a href=\"https://wallstreetcn.com/articles/3720987\">网页链接</a>\n\n</div>\n\n\n</article>\n</div>\n</body>\n</html>\n","isBrief":false,"type":0,"news_type":1,"symbol":"SG9999002224.SGD","symbol_name":"Allianz Global High Payout 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